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Argye Hillis MD, MA
Argye Elizabeth Hillis MD, MA Associate Editor
Nina Schor MD, PhD
Nina F. Schor MD, PhD Advisory Board
Marinos Dalakas MD, FAAN
Marinos C. Dalakas MD, FAAN Advisory Board
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Published in Neurology

Journal Scan / Research · October 15, 2020

Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With DMD

JAMA Neurology

 

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JAMA Neurology
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy: A Nonrandomized Controlled Trial
JAMA Neurol 2020 Sep 01;7(9)1122-1131, JR Mendell, Z Sahenk, K Lehman, C Nease, LP Lowes, NF Miller, MA Iammarino, LN Alfano, A Nicholl, S Al-Zaidy, S Lewis, K Church, R Shell, LH Cripe, RA Potter, DA Griffin, E Pozsgai, A Dugar, M Hogan, LR Rodino-Klapac

From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.

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