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Gene Therapy for Leber's Congenital Amaurosis
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The New England Journal of Medicine
From MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.
Long-Term Effect of Gene Therapy on Leber’s Congenital Amaurosis
N. Engl. J. Med 2015 May 14;372(20)1887-1897, JW Bainbridge, MS Mehat, V Sundaram, SJ Robbie, SE Barker, C Ripamonti, A Georgiadis, FM Mowat, SG Beattie, PJ Gardner, KL Feathers, VA Luong, S Yzer, K Balaggan, A Viswanathan, TJ de Ravel, I Casteels, GE Holder, N Tyler, FW Fitzke, RG Weleber, M Nardini, AT Moore, DA Thompson, SM Petersen-Jones, M Michaelides, LI van den Born, A Stockman, AJ Smith, G Rubin, RR AliFrom MEDLINE®/PubMed®, a database of the U.S. National Library of Medicine.